FDA Guidance for Industry: Pediatric Rare Diseases — A Collaborative Approach for Drug Development Using Gaucher Disease as a Model
Title:
FDA Guidance for Industry: Pediatric Rare Diseases —
A Collaborative Approach for Drug Development Using Gaucher Disease as a Model
Origin/Publisher:
FDA, https://www.fda.gov/downloads/Drugs/GuidanceComplianceRegulatoryInformation/Guidances/UCM587660.pdf
Content:
The purpose of this guidance is to facilitate drug development in pediatric rare diseases.